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Title Agios’s Mitapivat (AG348) Mechanism of Action- Mellalta Meets findings
URL https://mellalta.com/agioss-pkr-activator-mitapivats-strategy-for-sickle-cell-disease-scd/
Category Fitness Health --> Conditions and Diseases
Meta Keywords Hemolytic anemia; Pyruvate kinase deficiency; Red Cell Enzyme Abnormalities; Red Cells; Treatment of pyruvate kinase deficiency, Agio pharmaceutical, EHA, Sickle cell disease, SCD, USFDA, PKR Thalassemia
Meta Description Mitapivat (AG348) Mechanism of Action
Owner Emma Stones
Description
Agios Pharmaceuticals, shared the proof of clinical concept that has been established based on preliminary analysis in the phase 1 study of mitapivat (AG-348) in patients with sickle cell anemia.